PTC Therapeutics closes acquisition of Sangamo's ST-920 Fabry gene therapy
The one-time AAV gene therapy is headed toward a rolling BLA submission expected to finish in the fourth quarter of 2026.
SEC filing
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The one-time AAV gene therapy is headed toward a rolling BLA submission expected to finish in the fourth quarter of 2026.
SEC filing
PTC will pay Sangamo $111 million at closing and could owe up to $100 million more tied to FDA approval milestones for ST-920.
SEC filing
PTC agreed to pay $111 million upfront plus up to $100 million in milestones for the BLA-stage AAV gene therapy, with a rolling FDA submission targeted for the fourth quarter of 2026.
SEC filing
Sephience sales drove product revenue growth as the company reported net income and advanced its Huntington's disease and Friedreich's ataxia programs.
SEC filing